Resources Category: Publications

Publications
Advancing Amyloidosis: A Research Roadmap
The white paper contains the highest priorities and a research framework for the systemic amyloidosis diseases. This consensus document was developed through a rigorous process with the participation of 71 international experts from academic, clinical, regulatory, patient advocacy, health policy, industry, and other key areas. This publication is intended to identify improve and accelerate a drug development pathway for the systemic amyloidosis diseases.
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Publications
Publications
Voice of the Patient Report
A comprehensive report submitted to the FDA in 2016 by ARC. This is a detailed summary of the patient testimony presented at the Patient-Focused Drug Development meeting. This report will serve a critical function in communicating to both FDA review staff and industry the improvements that patients want and hope to see in their daily lives.    
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Publications
Publications
Rationale, Application and Clinical Qualification for NT-proBNP as a Surrogate End Point
Published: Leukemia, July 2016 | Author: G Merlini et al.
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Publications
Publications
Light Chain Amyloidosis Patient Experience Survey
Published: Advances in Therapy, 2015 | Author: I Lousada et al.
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Publications
Publications
ARC Cardiac Amyloidosis Survey: Results From AL Patients and Caregivers
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Publications
Publications
Guidance for Industry AL Amyloidosis – Developing Drugs for Industry
Developing the guidance involved active participation from all stakeholder groups including patients, medical experts, academics and biopharmaceutical industry representatives. This guidance has been submitted to FDA.
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Publications

AMYLOIDOSIS RESEARCH CONSORTIUM, INC.
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